A novel glycotechnology to produce human lysosomal enzymes carrying synthetic N-glycans with terminal mannose 6-phosphate residues and application to enzyme placement therapy for lysosomal diseases

作者:Itoh Kohji; Nishioka So Ichiroh; Kobayashi Isao; Matsuzaki Yuji; Iino Kenta; Nadanaka Satomi; Kasashima Sumitani Megumi; Hidaka Tomo; Tsuji Daisuke; Sezutsu Hideki; Kitagawaa Hiroshi; Yamamoto Kenji
来源:We're Organizing Research for Lysosomal Diseases (WORLD) Symposium, 2018-02-05 To 2018-02-09.
DOI:10.1016/j.ymgme.2017.12.169