An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A (vol 9, 199, 2014)

Attarian Shahram; Vallat Jean Michel; Magy Laurent; Funalot Benoit; Gonnaud Pierre Marie; Lacour Arnaud; Pereon Yann; Dubourg Odile; Pouget Jean; Micallef Joelle; Franques Jerome; Lefebvre Marie Noelle; Ghorab Karima; Al Moussawi Mahmoud; Tiffreau Vincent; Preudhomme Marguerite; Magot Armelle; Leclair Visonneau Laurene; Stojkovic Tanya; Bossi Laura; Lehert Philippe; Gilbert Walter; Bertrand Viviane; Mandel Jonas; Milet Aude; Hajj Rodolphe; Boudiaf Lamia

doi:10.1186/s13023-016-0463-6

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An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A (vol 9, 199, 2014)

作者：Attarian Shahram; Vallat Jean Michel; Magy Laurent; Funalot Benoit; Gonnaud Pierre Marie; Lacour Arnaud; Pereon Yann; Dubourg Odile; Pouget Jean; Micallef Joelle; Franques Jerome; Lefebvre Marie Noelle; Ghorab Karima; Al Moussawi Mahmoud; Tiffreau Vincent; Preudhomme Marguerite; Magot Armelle; Leclair Visonneau Laurene; Stojkovic Tanya; Bossi Laura; Lehert Philippe; Gilbert Walter; Bertrand Viviane; Mandel Jonas; Milet Aude; Hajj Rodolphe; Boudiaf Lamia

来源：Orphanet Journal of Rare Diseases, 2016, 11(1): 92.

DOI：10.1186/s13023-016-0463-6