A PRAGMATIC TRIAL OF DELAYED-RELEASE CYSTEAMINE BITARTRATE IN CHILDREN LESS THAN 6 YEARS OLD WITH CYSTINOSIS

作者:Langman Craig B; Greenbaum Larry; Grimm Paul; Elenberg Ewa; Deschenes Georges; Niaudet Patrick; Morin Denis; Checani Gregg
来源:53rd ERA-EDTA Congress, 2016-05-21 to 2016-05-24.