Stem cell transplantation for tetratricopeptide repeat domain 7A deficiency: long-term follow-up

作者:Kammermeier Jochen; Lucchini Giovanna; Pai Sung Yun; Worth Austen; Rampling Dyanne; Amrolia Persis; Silva Juliana; Chiesa Robert; Rao Kanchan; Noble Jamieson Gabriele; Gasparetto Marco; Ellershaw Drew; Uhlig Holm; Sebire Neil; Elawad Mamoun; Notarangelo Luigi; Shah Neil; Veys Paul*
来源:Blood, 2016, 128(9): 1306-1308.
DOI:10.1182/blood-2016-01-696385