ALN-TTR, AN RNAI THERAPEUTIC FOR THE TREATMENT OF TRANSTHYRETIN (TTR) AMYLOIDOSIS, MEDIATES REGRESSION OF PERIPHERAL TTR PROTEIN DEPOSITS IN A TRANSGENIC MOUSE MODEL

作者:Alvarez Rene; Borland Todd; Costelha Susete; Chen Qingmin; Nechev Lubomir; Jeffs Lloyd B; Sah Dinah W; Saraiva Maria Joao
来源:61st Annual Meeting of the American-Association-for-the-Study-of-Liver-Diseases, 2010-10-29 to 2010-11-02.
  • 出版日期2010-10