Use of 2 hydroxypropyl-beta-cyclodextrin therapy in two adult Niemann Pick Type C patients

作者:Alejandra Garcia Robles Ana; Jose Company Albir Maria; Eduardo Megias Vericat Juan; Jose Fernandez Megia Maria; Carlos Perez Miralles Francisco; Lopez Briz Eduardo; Alcala Vicente Carmen; Galeano Inmaculada; Casanova Bonaventura; Luis Poveda Jose
来源:Journal of the Neurological Sciences, 2016, 366: 65-67.
DOI:10.1016/j.jns.2016.04.048