A Phase 2/3 Study of the Efficacy and Safety of Ex Vivo Gene Therapy with Lenti-DTM Lentiviral Vector for the Treatment of Cerebral Adrenoleukodystrophy

作者:Eichler Florian S; Duncan Christine; Amartino Hernan; Aziz Bose Razina; Baruchel Andre; Dansereau Colleen; Dalle Jean Hugues; Gaspar H Bobby; Gissen Paul; Kohn Donald B; Larghero Jerome; Lund Troy C; Miller Weston P; Musolino Patricia L; O'Meara Tara; Orchard Paul J; Paker Asif M; Shah Ami J; Shamir Esther; Raymond Gerald V; Sankar Raman; Smith Nicholas J C; Thrasher Adrian J; Aubourg Patrick; Williams David A
来源:19th Annual Meeting of the American-Society-of-Gene-and-Cell-Therapy (ASGCT), 2016-05-04 to 2016-05-07.
  • 出版日期2016-5